Study evaluates safety and dosing of siRNA moleculeResearchers are testing a small interfering RNA molecule designed to reduce prion protein production. This marks the first human trial for this treatment.
HackerNews frontBiotech
- Field
- drugs and trials
- What they did
- Researchers have started phase 1 clinical trials for a new drug candidate that uses small interfering RNA to reduce the level of prion protein causing the disease.
- Why it matters
- This will help determine the safety and correct dosage of the medicine to see if it should move to larger trials with more patients.
#prion disease#sirna#clinical trial#neurodegenerative disorder
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